Nusinersen treatment in 68 children with 5q spinal muscular atrophy: A case series report
MA Kai, GUO Xiaohua, YU Chunmei, JIN Ruifeng, LIU Fangfang, GAO Min
Chinese Journal of Evidence-Based Pediatrics . 2023, (4): 286 -290 .  DOI: 10.3969/j.issn.1673-5501.2023.04.008