诺西那生钠治疗5q型脊髓性肌萎缩患儿68例病例系列报告
马凯 郭晓华 于春梅 金瑞锋 刘芳芳 高敏
Nusinersen treatment in 68 children with 5q spinal muscular atrophy: A case series report
MA Kai, GUO Xiaohua, YU Chunmei, JIN Ruifeng, LIU Fangfang, GAO Min
中国循证儿科杂志
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2023, (4): 286
-290
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DOI: 10.3969/j.issn.1673-5501.2023.04.008